Compromised Catalysis and Potential Folding Defects in in Vitro Studies of Missense Mutants Associated with Hereditary Phosphoglucomutase 1 Deficiency*

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Summary

The first in vitro biochemical characterization of 13 missense mutations involved in PGM1 deficiency shows compromised catalysis and differential effects on recombinant protein folding/stability are found, suggesting both protein misfolding and catalytic impairment may play a role in the disorder.

Type
article
Published
2014-10-06
Cited by
45
References
34
Access
Open access

Keywords

Mathematical economics, Economics, Computer science, Neoclassical economics

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