Gene therapy for severe combined immunodeficiency.

Keywords

Humanities, Philosophy, Physics

References

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• Bone marrow gene transfer in three patients with adenosine deaminase deficiency.Peter M. Hoogerbrugge, Victor W. van Beusechem, Alain Fischer — 1996
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• TTG-2, a new gene encoding a cysteine-rich protein with the LIM motif, is overexpressed in acute T-cell leukaemia with the t(11;14)(p13;q11).Brigitte Royer‐Pokora, Ursula Loos, W. D. Ludwig — 1991
• Update on treatment of human SCID-X1 by somatic gene therapy using a pseudotyped gammaretroviral vectorHB Gaspar, Kate Parsley, S Howe — 2004
• Stable and functional lymphoid reconstitution of common cytokine receptor gamma chain deficient mice by retroviral-mediated gene transfer.Claire Soudais, Shiho Tsujino, Lama I. Sharara — 2000
• T Cell Repertoire Development in Humans with SCID After Nonablative Allogeneic Marrow Transplantation 1Marcella Sarzotti, Dhavalkumar D. Patel, Xiaojing Li — 2003
• Mutations in the tyrosine phosphatase CD45 gene in a child with severe combined immunodeficiency diseaseChun Kung, Jeanette T. Pingel, Markku Heikinheimo — 2000
• MHC class II deficiency: a disease of gene regulation.Jean Villard, Krzysztof Masternak, Barbara Lisowska‐Grospierre — 2001
• Gene Therapy Insertional Mutagenesis InsightsUtpal P. Davé, Nancy A. Jenkins, Neal G. Copeland — 2004
• Spontaneous in vivo reversion to normal of an inherited mutation in a patient with adenosine deaminase deficiencyRochelle Hirschhorn, Diana Ruixi Yang, Jennifer M. Puck — 1996
• Lack of dominant-negative effects of a truncated gamma(c) on retroviral-mediated gene correction of immunodeficient mice.Makoto Otsu, Kazuo Sugamura, Fabio Candotti — 2001
• Diversity, functionality, and stability of the T cell repertoire derived in vivo from a single human T cell precursor.Philippe Bousso, V. Wahn, Iyadh Douagi — 2000
• Position-effect protection and enhancer blocking by the chicken β-globin insulator are separable activitiesFélix Recillas‐Targa, Michael J. Pikaart, Bonnie Burgess-Beusse — 2002
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• Immunological reconstitution of sex-linked lymphopenic immunological deficiency.RichardA. Gatti, HilaireJ. Meuwissen, HughD. Allen — 1968
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Cited by

• Shock wave-induced permeabilization of mammalian cells.Rohit Sunkam Ramanujam — 2018
• Gene therapy for Athabascan SCIDMegan M. Multhaup — 2010
• LA NICHE ÉCOLOGIQUE: CONCEPTS, MODÈLES, APPLICATIONSArnaud Pocheville — 2010
• Enhanced Gene Delivery Mediated by Incorporation of Recombinant Fusion Proteins: Listeriolysin O and Peptides Derived from Protamine.Hyun‐Na Koo — 2011
• Chromosomal integration in vitro and in vivo of high capacity adenoviral vectorsSam L. Stephen — 2007
• Développement de vecteurs lentiviraux régulables pour le transfert de gène dans le système nerveux centralLahouari Amar — 2007
• The fetal respiratory system as target for antenatal therapyJaan Toelen, Marianne Carlon, Filip Claus — 2011
• The interdependence between biological and ethical analyses of safety and efficacy in translational gene therapyC. Deakin — 2013
• Etude et Développement de Vecteurs Synthétiques pour la Délivrance d'Oligonucléotides à visée thérapeutique.Sarah Resina — 2007
• Investigation of the effects of virus integration on host gene expression in mouse tumour samplesEmma Osejindu — 2011
• The quest for new improved adenovirus gene therapy vectors against glioma tumoursJohan Skog — 2005
• Estudio inmunológico de las inmunodeficiencias primarias de células T y BM. García-Rodríguez, Gumersindo Fontán-Casariego — 2006
• The use of retroviral vectors for gene transfer into hematopoietic stem cells.Jeff Holst, John E.J. Rasko — 2006
• Use of murine models to test novel gene transfer strategies for the treatment of fanconi anemiaAnna C. Leath — 2010
• Treatment of an infant with X‐linked severe combined immunodeficiency (SCID‐X1) by gene therapy in AustraliaSamantha L. Ginn, Julie Curtin, Christine M. Smyth — 2005
• Targeted delivery of biological agents.Jenny A. Greig — 2009
• Implications for Gene Therapy-Limiting Expression of IL-2Rγc Delineate Differences in Signaling Thresholds Required for Lymphocyte Development and MaintenanceSelinda J. Orr, Stephen Roessler, Laura Quigley — 2010
• Strategy of oral vaccination by polymeric nanoparticles : M cell targeting or bioadhesionLaurence Plapied — 2011
• Cell and tissue engineering and clinical applications: An overviewJ.F. Stoltz, David Bensoussan, V. Decot — 2006
• CUESTIONAMIENTOS ÉTICOS RELACIONADOS CON LA TERAPIA GÉNICA PARA EL TRATAMIENTO DE ENFERMEDADES HEREDITARIASJosé Henry Osório — 2011

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